New research identified a stable ATP-binding human noncoding RNA that could advance RNA therapeutics by revealing new ways to ...

All cells in the human body—and the motions they enable, from our beating hearts to our wiggling toes—use energy generated by ...

Super-enhancers are a specialized class of functional, non-coding RNA molecules transcribed directly from regions of the ...

Researchers at Carnegie Mellon University in Qatar (CMU Q) have discovered a genetic molecule that could provide new ...

The FDA has granted HAYA Therapeutics Fast Track Designation for HTX-001 for the treatment of symptomatic nonobstructive hypertrophic cardiomyopathy.

The FDA granted Fast Track designation to HTX-001, an investigational lncRNA-targeting antisense therapy for nonobstructive hypertrophic cardiomyopathy.

Manufacturers of a non-invasive saliva test say it can accurately diagnose endometriosis, but Australian experts warn there ...

HTX-001 has not received approval from the FDA, European Medicines Agency, or any other regulatory authority.

Researchers have identified a set of 34 circular RNAs in blood that can detect Alzheimer’s disease with striking accuracy and ...

Rugonersen, a potentially best-in-class antisense oligonucleotide (ASO) therapy in development for Angelman syndrome, advanced into the pivotal ...

Design Therapeutics' DT-216P2 showed 6.4-point mFARS gains in Friedreich’s ataxia, but data is early. Click here to read the ...

With AI, it's now possible for researchers to predict the three-dimensional structures of proteins directly from their amino-acid sequences. But what biologists really want to predict, says Columbia ...