Biomarker-driven approaches enhance the likelihood of identifying optimal patient populations and streamline trials through accelerated approval pathways, with FDA approvals incorporating increasingly ...

An international team led by Monash University researchers has uncovered the genetic code governing the way genetic mutations affect mRNA and result in disease.

Some genetic disorders—such as cystic fibrosis, hemophilia and Tay Sachs disease—involve many mutations in a person's genome, ...