Scientists cured sickle cell. Then their next challenge began.

Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these personalized treatments faster, cheaper, and available to far more patients.
The Well News on MSN

FDA approves first gene therapy technology to treat children with sickle cell disease

WASHINGTON - The Food and Drug Administration Wednesday granted supplemental approval for a breakthrough CRISPR gene therapy medication, making it the first available to treat young children with ...
Forbes

Hope And Hurdles For Sickle Cell Gene Therapy

Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine This voice experience is generated by AI. Learn more. This ...
Medscape

Scotland Approves Gene Therapy for Sickle Cell Disease

The Scottish Medicines Consortium (SMC) has accepted exagamglogene autotemcel (Casgevy, Vertex Pharmaceuticals) for use within NHS Scotland to treat sickle cell disease (SCD) in patients aged 12 years ...
News on 6

New gene therapies offer hope for sickle cell patients

Doctors say new gene-based treatments could offer long-term relief — and possible cures — for people living with sickle cell disease. Sickle cell disease has long shortened lives in the United States, ...

FDA expands use of first sickle cell disease gene therapy for children as young as 2 years

The U.S. Food and Drug Administration has issued a supplemental approval for Casgevy (exagamglogene autotemcel) for patients ...
The Advocate

First Louisiana patient to receive sickle cell gene therapy heads home after 6 weeks in hospital

The first patient in Louisiana to receive genetically edited therapy for sickle cell disease went home this week after months in isolation at Manning Family Children's Hospital in New Orleans. Daniel ...
Acsh.org

Sickle Cell, Gene Therapy, and the Limits of Medical Triumph

Gene therapy has given sickle cell disease what medicine has long promised but rarely delivered: the possibility of a cure. Yet the slow uptake of Casgevy and Lyfgenia shows that even dazzling science ...
Healthline

Louisiana Man Becomes First In Region to Be Functionally Cured of Sickle Cell Disease

Share on Pinterest A Louisiana man has become the first in the Gulf South to be functionally cured of sickle cell disease using gene therapy. Image Credit: Marti Sans/Stocksy Daniel Cressy of ...

At 23, he was functionally cured of sickle cell. Now he's ready to fly.

Daniel Cressy's illness was a barrier to getting his pilot's license, until a novel treatment was approved in the United ...